Transient Transfection Methods for Clinical Adeno-Associated Viral Vector Production
نویسندگان
چکیده
منابع مشابه
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Duchenne muscular dystrophy (BMD) is an inherited X-link disease. The incidence of this muscle-wasting disease is 1:5000 male live births. Mutation in the gene coding for dystrophin is the main cause of BMD. Most cases of this disease succumb to respiratory and cardiac failure in 3rd to 4th decades. The slow progression of BMD and recent achievement of gene therapies make it as an appropriate c...
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ژورنال
عنوان ژورنال: Human Gene Therapy
سال: 2009
ISSN: 1043-0342,1557-7422
DOI: 10.1089/hum.2009.064